synapticfire

5 ms·

1. 1.▲
   by synapticfire 10y ago

   I know of no other gene therapies, but other treatments are very real, and very close to being approved. My son is in a trial of nusinersen with Ionis Pharmaceuticals. The results of this drug are astounding.
2. 2.▲
   by synapticfire 10y ago

   I believe with so called "Orphan diseases" the economics of research and eventual market release rarely work out for private companies. I believe it takes a research phase funded by charities, grants, and tax breaks for companies
3. 3.▲
   by synapticfire 10y ago

   Another promising gene therapy, close to being submitted to the FDA for approval, has been developed by Ohio State University, Nationwide Children's hospital, and Avexis for the treatment, and possibly cure, of Spinal Muscular Atrophy.
4. 4.▲
   by synapticfire 12y ago

   Rarely are the prices different if paying in cash vs credit (due to agreements I believe) which means you still pay the extra 3 to 5 percent, but receive no reward points, cash back, or anything extra. So in affect, by paying cash, you are
5. 5.▲
   by synapticfire 13y ago

   Tesla requested the investigation. I didn't read a claim about being poorly treated. (I am not saying that such a claim does not exist.) "Second, we have requested that the National Highway Traffic Safety Administration conduct a