notahackeratll

5 ms·

1. 1.▲
   by notahackeratll 5mo ago

   This is not linked to MFN pricing, which only impact Praulant…(PCSK9 for hypercholesterolemia)
2. 2.▲
   by notahackeratll 5mo ago

   This was not a political decision. These kind of accelerated paths have been available for years for a wide variety of therapies.
3. 3.▲
   by notahackeratll 5mo ago

   I would think the time frame is not nearly as long as that… hopefully
4. 4.▲
   by notahackeratll 5mo ago

   Consider this from the perspective of a deaf person. While it seems silly from the perspective of a hearing person, a lot of people in the deaf community are concerned that they are viewed as having a problem needing to be fixed, rather tha
5. 5.▲
   by notahackeratll 5mo ago

   Yes, some of the vector was likely cleared from the AH and exposed the contra lateral eye
6. 6.▲
   by notahackeratll 5mo ago

   Patients with fever induced hearing loss regardless of OTOF mutations were specifically excluded (see inclusion criteria on clinical trials.gov for NCT05788536). With regard to your point about shedding or systemic exposure. If non function