7 ms·
Would the DEC2 mutation be amenable to being given to adults via a gene therapy?
by jonmrodriguez 11y ago
Would the DEC2 mutation be amenable to being given to adults via a gene therapy?
- imaginenore 11y agoI don't think anybody here is capable of answering that. We simply haven't tried anything like that on humans. We have the technology called CRISPR/Cas, which was used (successfully) to cure adult mice of genetic liver disease. https://en.wikipedia.org/wiki/CRISPR https://en.wikipedia.org/wiki/CRISPR